a rare genetic neurological disorder that is first recognized in infancy and primarily occurs in girls, but there are rare cases reported in boys as well. Rett syndrome leads to severe impairments, affecting nearly every aspect of the person's life.
Rare, but not alone
Rett syndrome is a rare disease that impacts about 350,000 people worldwide and about 11,000 people in the United States. Rett syndrome is the second most common cause of severe intellectual disability in females and during its period of developmental regression, a substantial proportion of affected individuals meet diagnostic criteria for autism spectrum disorder (ASD).
Clinical research studies (also called clinical trials) are critical for identifying new ways of treating medical conditions and diseases. All therapeutics must be tested in clinical research studies before they can be approved and prescribed to people.
Clinical research studies can help advance the understanding of a disease. All clinical research studies rely on individuals volunteering to participate.
By joining the ANAVEX2-73 Rett Syndrome study your loved one has the opportunity to help advance clinical research into Rett syndrome.
By joining a clinical study you might have the opportunity to:
Better understand your or your loved one's condition
Have your loved one's condition closely monitored
Help others living with Rett syndrome in the future